Impact

There has been tremendous progress in the understanding of potential causes of neurodegenerative diseases, however there are few treatment options available for patients. While considerable drug development efforts have gone into targeting pathologies such as amyloid beta, tau, and a-synuclein, we believe that additional novel approaches are necessary to truly make a difference in neurodegenerative disease.

Harnessing a deep understanding of the critical role that that lysosomal biology plays in neurodegeneration, we are driving the discovery of medicines with the potential to address disease at the cellular level and positively change the trajectory of neurodegenerative disease.